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Mark A. Kay, M.D., Ph.D.

Academic Appointments

  • Dennis Farrey Family Professor in Pediatrics, and Professor of Genetics

Key Documents

Contact Information

  • Academic Offices
    Personal Information
    Email Tel (650) 498-6531
    Alternate Contact
    Melinda Hing Administrative Associate Tel Work 650-498-6532


Academic Appointments

Administrative Appointments

  • Associate Chair for Basic Research, Department of Pediatrics (2012 - present)
  • President, American Society of Gene Therapy (2005 - 2006)
  • President Elect, American Society of Gene Therapy (2004 - 2005)
  • Chair of Organizing Committee, Gordon Conference on Viral Vectors for Gene Therapy (2003 - 2004)
  • Vice President, ASGT (2003 - 2004)
  • Chief Scientific Advisor, Benitec, LLC (2003 - 2005)
View All 8administrative appointments of Mark Kay

Honors and Awards

  • Sam Rosenthal Prize for Excellence in Pediatrics, Rosenthal Foundation (2011-2013)
  • Outstanding Achievement/Investigator Award, American Society for Cell and Gene Therapy (2013)
  • Elected Member, AAP (2010)
  • Researcher of the Year, National Hemophilia Foundation (2000)
  • Pediatric Researcher of the Year, E. Mead Johnson Award (2000)
  • Elected Member, American Society for Clinical Investigation (1997)
View All 8honors and awards of Mark Kay

Professional Education

B.S.: Michigan State University, Physical Sciences (1980)
Ph.D.: Case Western Reserve University, Developmental Genetics (1986)
M.D.: Case Western Reserve University (1987)

Research & Scholarship

Current Research and Scholarly Interests

The goal of the Program in Human Gene Therapy is to develop gene transfer technologies and use them for hepatic gene therapy for the treatment of genetic and acquired diseases. The general approach is to develop new vector systems and delivery methods, test them in the appropriate animal models, uncover the mechanisms involved in vector transduction, and use the most promising approaches in clinical trials. Specifically, we work on a variety of viral and non-viral vector systems. Our major disease models are hemophilia, hepatitis C and B viral infections, and diabetes. The second major focus includes the role that small RNAs play in mammalian gene regulation.




Graduate and Fellowship Program Affiliations



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Publication Topics

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